Gene silencing medicine transforms crippling pain

An innovative type of medicine – called gene silencing – is set to be used on the NHS for people who live in crippling pain. The drug treats acute intermittent porphyria, which runs in families and can leave people unable to work or have a normal life. Clinical trials have shown severe symptoms were cutContinue reading “Gene silencing medicine transforms crippling pain”

Gene therapy: ‘Now I can see my own face again

Jake Ternent has been gradually losing his central vision since birth, because of a rare inherited genetic eye condition. And, despite the pandemic, 2020 was a landmark year for the 24-year-old, from County Durham, who became the first person in the UK to receive a revolutionary new gene therapy on the NHS. His condition –Continue reading “Gene therapy: ‘Now I can see my own face again”